Vaccinex’s Phase 2 SIGNAL study, evaluating the investigational antibody pepinemab (VX15/2503) in Huntington’s disease patients with late prodromal and early disease, is ongoing and has tested pepinemab in all 265 patients enrolled in cohort B, the company announced. As of March 31, only 37 patients in this group…
I have pink eye. Again. And I’m extremely happy I got it. I’ll get to why in a moment, but first some background. For the third time since March, the whites of my eyes are red and watery with occasional discharges that result in some crusting on my eyelashes.
While the ongoing COVID-19 pandemic won’t have much of an impact on cash available for new biotech startups, it has begun to cause delays in the development of gene therapies to treat a variety of rare diseases. That’s the consensus of industry experts who spoke in a May 26 webinar…
If you’ve ever experienced an allergic reaction to something, you probably understand why the root word of misery comes from the Latin word “miseria,” which means wretchedness. My dog has been in a state of misery for the past two weeks due to an allergic reaction. We don’t know…
Teva Pharmaceuticals’ Austedo (deutetrabenazine tablets) has been approved by China’s National Medical Products Administration (NMPA) for treating chorea associated with Huntington’s disease and tardive dyskinesia…
European authorities must step up efforts to screen babies for a multitude of genetic disorders, a panel of experts suggested during a May 14-15 online medical conference. The session was part of the 10th European Conference on Rare Diseases & Orphan Products (ECRD2020) — which was to have occurred…
Working remotely, while slightly draining, has had its benefits. Being able to sleep in until the last possible second (and maybe sometimes slightly past that) and my ability to work anywhere are among them. That latter perk means I’ve been able to work from my parents’…
My husband and I were driving along a country road with no destination in mind. We needed to escape the city and our lives for the day. We drove past fields of tall, golden grass waving in the breeze, and turned down random roads that we happened upon. We cracked…
Eurordis, a Paris-based coalition of national rare disease associations across Europe, hosted its first all-virtual conference, bringing some 1,500 delegates from 57 countries together online during the COVID-19 pandemic. The 10th European Conference on Rare Diseases & Orphan Products (ECRD2020) — which was set for May 14–15 in…
Reality bites. That was the name of a 1994 romantic comedy movie starring Winona Ryder and Ethan Hawke. It’s about four recent graduates finding out how difficult life can be when searching for a decent job and true love after college. In pop culture, that phrase eventually came to…
Get regular updates to your inbox.
