Updates

February 21, 2019February 21, 2019
Cannabinoid-Based Treatment for Huntington’s Granted Orphan Drug Designation by FDA

tMMJ-002, a cannabis investigational product for the treatment of Huntington’s disease, has been granted Orphan Drug designation by the U.S. Food and Drug Administration, announced its developer MMJ ... Read more
February 21, 2019February 20, 2019
Vienna to Host RARE2019 Meeting on Rare Diseases

About 100 scientists, researchers, pharmaceutical executives, and others will converge on Austria’s capital city early next month for the 2nd International Congress on Advanced ... Read more
February 19, 2019February 19, 2019
Emotional Recognition Defect Linked to Apathy in Huntington’s, Study Shows

Impairment in emotional recognition — the process of identifying human emotion, most typically from facial expressions, particularly happy ones — seems to be linked ... Read more
February 14, 2019February 14, 2019
Researchers Get $6 Million to Continue Work on Huntington’s Stem Cell Therapy

In support of ongoing development of a prospective new therapy for Huntington’s disease, the California Institute for Regenerative Medicine (CIRM) has awarded University of ... Read more
February 12, 2019February 12, 2019
Fast Screening Strategy Identifies Potential New Inhibitors for Huntington’s Disease

Several small molecules have been identified by the Alborada Drug Discovery Institute as potential inhibitors to help halt the underlying mechanisms that drive the development of neurodegenerative ... Read more

News

Patients, Family and Friends to Take Part in Variety of Rare Disease Day Events Worldwide
February 11, 2019
Scores of events are afoot worldwide to mark Feb. 28, Rare Disease Day 2019. The activities ...
News

Impaired Glial Cell Development Contributes To Huntington’s, Mouse Study Suggests
February 7, 2019February 7, 2019
Dysfunction in the development and maturation of the brain’s primary support cells, know as ...
News

Phase 3 Trial of RG6042 Will Gauge Potential of Gene-silencing Approaches for Huntington’s, Other Diseases
February 5, 2019February 5, 2019
The upcoming Phase 3 trial of RG6042 will test whether lowering the levels of ...
News

Huntington’s Patients in US and Canada Being Enrolled in Phase 3 Study of RG6042
January 31, 2019February 1, 2019
A Phase 3 clinical trial is enrolling adults with Huntington’s disease across the United ...
News

FDA Clears First Clinical Study of AMT-130 Gene Therapy in Huntington’s disease
January 29, 2019January 29, 2019
uniQure is launching a Phase 1/2 trial in the United States to evaluate the ...
News

Brain Neurons Disconnect from Each Other in Process Called Neuritosis, Mouse Study of Huntington’s Reveals
January 24, 2019January 24, 2019
The progressive death of brain nerve cells observed in Huntington’s disease is likely preceded by ...

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Enrollment Completed for Phase 2 Trial Testing VX15/2503 in Early and Late Prodromal Huntington’s Patients
January 22, 2019January 22, 2019
Vaccinex has completed its target enrollment in a Phase 2 clinical trial assessing the ...
Cerebellar Purkinje Cell Loss Linked to Huntington’s Motor Symptoms, Study Reports
January 17, 2019January 17, 2019
The loss of a type of nerve cell called a Purkinje cell in a ...
Asuragen Launches AmplideX as Faster Diagnostic Test for Huntington’s Disease
January 15, 2019January 15, 2019
Machine Learning Applied to EEG Data May Serve as Huntington’s Biomarker, Study Suggests
January 10, 2019January 10, 2019
Most Transplanted Fetal Nerve Cells in Brain of Huntington’s Patients Do Not Thrive, Study Says
January 8, 2019January 8, 2019
Huntexil Failed to Improve Motor Function of Huntington’s Patients in Phase 2 Trial
January 3, 2019January 3, 2019

Rising Healthcare Costs Strain EU Budgets Even as New Therapies Flourish
December 21, 2018December 20, 2018
Cash-strapped governments across the 28-member European Union are struggling to control runaway healthcare expenditures ...
Gait, Balance Problems Can Help Diagnose Late-Onset Huntington’s, Study Finds
December 20, 2018December 20, 2018
European Huntington Association Promotes Awareness, Potential Gene Therapies
December 13, 2018December 13, 2018
FDA Orphan Designation Moves Vybion’s Huntington’s Therapy Closer To Clinical Trial
December 6, 2018December 6, 2018

Young People Caring for Huntington’s Disease Parent Worry ‘This Could Be Me’
November 29, 2018November 30, 2018
Taking care of parents with Huntington’s disease evokes thoughts of “this could be me” in young ...
Compound in Raspberries May Help Protect Against Huntington’s, Other Neurodegenerative Diseases, Study Says
November 15, 2018November 15, 2018
Impaired Energy Metabolism Linked to Age of Onset in Huntington’s Patients, Study Shows
November 8, 2018November 8, 2018

News

Juvenile Huntington’s More Aggressive, Leads to Early Symptoms, Study Reports
November 1, 2018November 1, 2018
The juvenile form of Huntington’s disease, which affects patients younger than 20, is particularly aggressive ...
News

#NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach
October 29, 2018October 29, 2018
With the U.S. midterm elections now less than two weeks away, patient advocacy groups ...
News

DNA-based Therapy Reduces Anxious Behavior in Huntington’s Mouse Model, Study Shows
October 25, 2018October 25, 2018
Suppressing the expression of the defective huntingtin gene using antisense oligonucleotides lowered anxiety-like behavior in ...
News

Gene Therapy VY-HTT01 Can Protect Brain Cells from Damage Caused by HTT Faulty Gene, Results Show
October 23, 2018October 23, 2018
One-time delivery of Voyager Therapeutics’ lead candidate gene therapy, VY-HTT01, effectively reduced the levels of the ...
News

Advanced Huntington’s Patients Have Marked Difficulties in Driving, Study Shows
October 18, 2018October 18, 2018
Patients at advanced stages of Huntington’s disease have marked difficulties in controlling vehicles in ...
News

Neurological Dysfunction Detectable Before Huntington’s Diagnosis, Study Finds
October 15, 2018October 15, 2018
Signs of neurological dysfunction can start long before a clinical diagnosis of Huntington’s disease, a study ...
News

New Blood Test May Track Early Changes in Huntington’s Disease, Study Finds
October 11, 2018October 11, 2018
Two proteins present in the blood and brains of patients with Huntington’s disease may ...
News

Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments
October 9, 2018October 9, 2018
Half a year has gone by since disgraced pharma executive Martin Shkreli was sentenced ...
News

Northwestern University Receives $12.6 Million to Study Protein Balance Mechanisms in Health and Disease
October 9, 2018October 9, 2018
The National Institute on Aging at the National Institutes of Health (NIH) has granted ...

May 23, 2016May 23, 2016

Blocking 2 Enzymes Seen to Reduce Nerve Cell Loss in Fruit Fly Model of Huntington’s

News

A collaboration between researchers at the University of Leicester, U.K., and the University of Maryland School of Medicine, Baltimore, may lead to a way of reversing some symptoms of neurogedenerative diseases, like Huntington’s, by blocking two specific enzymes of the kynurenine ... Read more

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