News Early White Matter Alterations Are Clinically Relevant in Huntington’s Patients, Study Shows

News Experimental Huntington’s Treatment Improves Memory, Other Brain Functions in Mouse Study

News Laquinimod Fails to Improve Motor Function but Reduces Brain Atrophy in Phase 2 Huntington’s Trial

News PRIME Designation Should Help Promising Experimental Therapy Reach Huntington’s Patients Faster

News Protein May Help Prevent Nerve Cell Death in Huntington’s Disease

News Damage to Nuclear DNA Shown to Correlate with Huntington’s Duration, Patient’s Ability to Function

News Phase 2a Trial Investigates BP Medicine SOM3355 as Treatment for Chorea

News Genes Involved in Inflammation, Cellular Structure May Be Therapeutic Targets in Huntington’s

News Retrotope’s RT001 Reduced Cognitive Defects in Mice with Huntington’s Disease, Study Shows

News Improved Genetic Testing Protocols Should be Available for Huntington’s Disease, Study Contends

Leber's hereditary optic neuropathy, News Skyhawk, Celgene Partner to Develop Small Molecule Treatments for Huntington’s, Other Neurological Diseases

News Scotland’s Fife Launches Groundbreaking Local Care Frameworks for Huntington’s Disease

News Experts Seeking Tools to Assess Effectiveness of Targeted Huntington’s Therapies

News Dysfunction of Astrocyte Brain Cells Plays Key Role in Huntington’s, Mouse Study Suggests

Huntington's Disease News, News New Huntingtin Protein Strategy Significantly Improves Symptoms Over Time, Study Finds

News Defective Protein in Huntington’s Linked to Heart Dysfunction in Mouse Study

News Huntington’s Protein Levels in Saliva May Work as Biomarker for Disease Worsening, Study Suggests

News Novel Spotlights Daily Struggles of Patients and Families

News Program Provides Second Opinion About Rare Disease Diagnosis, Care

News Canada Trails US in Patient Access to Rare Disease Therapies, CORD President Says

News Huntington’s Seen to Start at Later Age in Patients with Arterial Hypertension, Study Finds

News US ‘Right to Try’ Law Meets with Mix of Praise and Criticism, Including Among Those with Rare Diseases

News Unexpected Link Between Huntington’s Disease and Rheumatoid Arthritis Found in Study

News #ECRD2018 – Genome Editing Might Be ‘Cure’ for Rare Diseases But Ethical Guidelines Needed, Panel Says

News Apathy Linked to Physical, Cognitive and Behavioral Disability in Huntington’s Patients, Study Finds

News #ERDC2018 – When Treating Rare Disease Patients, Don’t Overlook Quality of Life, Panel Urges

News Class of Lipids Merit ‘High Priority’ Attention as Possible Treatment Route in Huntington’s, Study Says

News #ERDC2018 – New EU Law to Protect Patient Data Could Affect Rare Disease Registries

News Antibiotic May Protect Huntington’s Nerve Cells from Death, Mouse Study Suggests

News AllianceRx Walgreens Prime and Walgreens Offer New Specialty Therapies, Including Austedo for Huntington’s

News ‘Rare Impact Awards’ Dinner Marks Orphan Drug Act and NORD at 35

News #ECRD2018 – EU Must Do More for Rare Disease Patients, Eurordis Leaders Say

News UK Group Leads Community-building Charge for Huntington’s Disease Awareness Week

News HDYO Works Through Camps, Education to Help Young People Affected by Huntington’s

News Blocking Gpr52 Receptor Improves Huntington’s Symptoms in Animal Models, Study Finds

News Iron Buildup in Mitochondria of Brain Cells May Promote Huntington’s Progression

News #ECRD2018 – Patient Access and Collaboration Focus of Eurordis Meeting May 10-12

News #AAN2018 – Potential Huntington’s Treatment Halts Loss of Brain Volume, Improves Metabolism, Study Finds

News #AAN2018 – IONIS-HTTRx Shows Promise in Phase 1/2 Trial to Treat Early-stage Huntington’s

News CHDI Foundation Joins PTC’s Quest to Develop Huntington’s Therapies

News NIH Agency Pioneers Collaborative Research into Rare Diseases

News HTT Mutations Seen to Cause Extensive Brain Remodeling, Affecting Motor and Cognitive Skills

News Immunotherapy Candidates Showing Promise as Potential Ways of Treating Huntington’s

News ‘Super Assassin’ of Cancer Cells Found in Huntington’s Disease Gene, Researchers Say

News Targeting Enzyme to Reduce Mutant Protein Levels May Be New Strategy to Fight Huntington’s, Study Says

News Cannabinoids Seen to Ease Motor Symptoms Like Dystonia in Early-onset Patients in Case Study

News Huntington’s and ALS Nonprofits Partner with Teva to Discover New Therapeutic Targets

News New Version of Genome Editing System Holds Potential to Treat Huntington’s

News Genome Sequencing and Its Clinical Potential Focus of NYC Rare Disease Day Event

News Strict Diet Control in Mouse Study Seen as Potential Huntington’s Disease Therapeutic Approach

News ‘A Disease May Be Rare, Hope Should Never Be,’ Says Boy with SMARD at Connecticut Rare Disease Day Event

News MMJ BioScience Licensed in Canada to Make Cannabis-based Medicine for Huntington’s Studies

News Rare Disease Groups Welcome FDA’s Embrace of ‘Real World’ Data in Clinical Trials

News US Lawmakers Urge Bipartisan Support for Rare Disease Research, Patients’ Needs

News IONIS-HTTRx Shows Promising Results in Phase 1/2 Clinical Trial

News HDSA Expands List of Huntington’s Disease Centers of Excellence to 43 for 2018

News Blocking Certain Glutamate Receptors Seen to Ease Huntington’s Advance in Mouse Model of Disease

News Tracking Nerve Cells’ Signaling-protein Delivery Is Shedding Light on Huntington’s

News Retrophin, Horizon Donate $3M Each to Rare Disease Institute at Children’s National

News Emerald Health’s Huntington’s Therapy Candidate EHP-102 Granted FDA Orphan Drug Status

News Huntington’s Patients’ Skin Cells Transformed Into Nerve Cells That Mimic Disease Symptoms

News BioNews to Cover 3 Rare Disease Day Events, Including NIH Conference

News Huntington’s Disease May Start Very Early in Embryo, Research Reveals

News Patient Advocacy Groups Worldwide Plan Events to Mark Rare Disease Day, Feb. 28

News Wave Life Sciences and Takeda Collaborating on Huntington’s Therapies

News Rare Disease Groups, Patients Differ on ‘Right to Try’ Bill Before US Congress

News Link Between Exact Mutation and Huntington’s Progression May Aid in Early Prognosis, Report Suggests

News Vaccinex Holding Business Opinion Leaders Luncheon on Huntington’s in New York City

News Physical Activity May Help Huntington’s Patients, Review Study Finds

News NORD Fundraiser Sets 7,000-Mile ‘Bike, Run or Walk’ Goal for 7,000 Rare Diseases

News Neurofeedback Training Boosts Brain Connections in Huntington’s, Despite Degeneration

News UniQure’s AMT-130 Granted Orphan Medicinal Product Status in Europe

News uniQure Aims to Begin First Human Trial of Investigational Gene Therapy AMT-130 for Huntington’s in 2018

News Strict Meal Schedule May Benefit Huntington’s Patients, UCLA Mouse Study Suggests

News MMJ Files US Patent for Cannabinoid-based Treatment for Huntington’s and MS

News Endurance Training May Delay Muscular Dysfunction in Huntington’s Patients, Study Shows

News Researchers Identify Markers to Track Huntington’s Years Before Signs of Disease

News Cancer Therapy Bexarotene Shows Early Promise in Treating Huntington’s, Mouse Study Finds

News Huntington’s Patients in UK Want to Open Debate on Assisted Dying, Small Study Shows

News Too Much Urea in Brain May Underlie Huntington’s Disease Progression, Study Shows

News Researchers Review Role of Manganese in Huntington’s Disease Development

News Roche Licenses Promising Huntington’s Therapy IONIS-HTTRx, Begins Extension Study

News Scientists Control Stem Cells’ Change to Neurons, a Potentially Valuable Tool for Huntington’s

News Activity and Levels of Enzyme Aco2 May Be Biomarker of Huntington’s Progression, Early Study Reports

News Taube Philanthropies Donates $750,000 to Buck Institute to Fund Huntington’s Research

News Rilmenidine Well-Tolerated in HD Patients, but More Studies Needed, Researchers Say

News Rare Disease Patient Groups Unite to Preserve Orphan Drug Tax Credit in US

News Hereditary Disease Foundation Gala Raises $900,000 for Huntington’s Research

News Spanish Study Explains Why Protein Loses Its Ability to Protect Nerve Cells

News Mitochon Pharmaceuticals Allowed First Patent Securing Development of MP101

News Canada’s ‘One Extra Push’ Campaign Aims to Raise Awareness of Huntington’s Disease

News Researchers Identify Mechanism to Prevent Toxic Accumulation of Proteins in Mitochondria

News Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’

News Natural Compounds May Carry Therapeutical Benefits for Huntington’s

News Plant Study Reveals Mechanism That May Explain Protein Folding in Human Disease

News uniQure Gene Therapy Candidate Improves Motor Coordination, Survival in Huntington’s Mice, Study Shows

News #NORDsummit – Alternatives to Large Placebo Trials, Grant Awards Among Ways FDA Supporting Rare Diseases, Chief Says

News Molecular Interactions Study May Advance Insight into Huntington’s Disease Processes

News #NORDsummit – Despite Criticism, Orphan Drug Act Is Working to Advance Needed Treatments, FDA Says

News European and North American Huntington’s Advocacy Groups Launch Joint Initiative