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January 16, 2020January 16, 2020

Vienna to Host European Conference on Huntington’s Disease in Mid-February

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As many as 80 experts from a dozen countries will gather next month in Vienna for the European Conference on Controversies in Huntington’s Disease (ECCH2020). The Feb. 13–14 meeting ... Read more

January 14, 2020January 14, 2020

Study of Brain Development in Those at Risk for Huntington’s Expands with $18M NIH Grant

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Efforts to understand brain development in young people at risk for Huntington’s disease have been given a boost by an $18 million grant awarded by the National Institute of ... Read more

January 7, 2020January 7, 2020

Investigational Compound Induces Significant Drop in Mutant Huntingtin Protein, Ongoing Trial Data Show

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Huntington’s patients who were treated with the compound WVE-120102 showed a statistically significant drop in mutant huntingtin protein (HTT) in their cerebrospinal fluid, according to a recent Phase 1b/2a ... Read more

January 2, 2020January 2, 2020

Selecting Right Mouse Model Key for Huntington’s Research, Therapy Development, Study Finds

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Certain aspects of Huntington’s disease (HD), such as the biologic mechanisms of depression, are not consistently replicated in mouse models of the disorder, which may hinder therapy development, a ... Read more

December 19, 2019December 19, 2019

Study Finds Abnormal Neural Development May Contribute to Huntington’s Disease, Offering New Therapeutic Strategy

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Abnormal development of neural tissues may precede neurodegeneration in early-onset juvenile forms of Huntington’s disease, a recent study has found. Researchers also showed how targeting the cellular pathway involved ... Read more

December 17, 2019December 17, 2019

MicroRNA May Help Prevent Buildup of Toxic Proteins in Huntington’s Disease, Study Shows

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A small RNA molecule known as microRNA-1, found in both worm and human cells, can promote the removal of toxic protein aggregates — hallmarks of neurodegenerative diseases — by ... Read more

December 12, 2019December 12, 2019

‘Co-produced’ Walking Group Beneficial for Patients, But Better Models Are Needed, Study Finds

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Joining a “co-produced” walking group can be beneficial for people with Huntington’s disease, increasing their confidence, strength, and ability to walk, a study found. However, further research is needed ... Read more

December 10, 2019

Gene Therapy Takes Center Stage at 2019 NORD Summit

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With so much recent publicity surrounding gene therapy, it’s no surprise that the topic was a major focus of the recent 2019 NORD Rare Diseases & Orphan Products Breakthrough ... Read more

December 10, 2019December 10, 2019

Poorer Ability to Recognize Face-like Objects Found in Presymptomatic Patients

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An inability to correctly identify face-like objects and fewer brain signals associated with facial recognition were found in people with Huntington’s disease who had yet to show symptoms, suggesting ... Read more

December 5, 2019

HHS Secretary Alex Azar Touts White House Efforts to Cure Rare Diseases

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Despite skyrocketing healthcare costs, President Trump is committed to protecting the 30 million or so Americans with rare diseases and ensuring timely, affordable access to lifesaving treatments, the nation’s ... Read more

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