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December 13, 2018December 13, 2018

European Huntington Association Promotes Awareness, Potential Gene Therapies

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There may be no cure yet for Huntington’s disease, but patients — and their families — can still do plenty to extend their life expectancy through proper diet, exercise, ... Read more

December 6, 2018December 6, 2018

FDA Orphan Designation Moves Vybion’s Huntington’s Therapy Closer To Clinical Trial

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A therapy for Huntington’s disease called INT41 was granted orphan drug designation by the U.S. Food and Drug Administration (FDA), bringing the treatment a step closer to being tested in ... Read more

November 29, 2018November 30, 2018

Young People Caring for Huntington’s Disease Parent Worry ‘This Could Be Me’

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Taking care of parents with Huntington’s disease evokes thoughts of “this could be me” in young caregivers and affects their planning for predictive genetic testing, a study shows. The study, ““This ... Read more

November 15, 2018November 15, 2018

Compound in Raspberries May Help Protect Against Huntington’s, Other Neurodegenerative Diseases, Study Says

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A bioactive compound present in raspberries called salidroside can prevent the cellular toxicity that occurs as a consequence of protein accumulation in certain neurodegenerative diseases, including Huntington’s disease, a study reports. ... Read more

November 8, 2018November 8, 2018

Impaired Energy Metabolism Linked to Age of Onset in Huntington’s Patients, Study Shows

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A deficiency in energy metabolism in the cells of patients with Huntington’s disease can partly explain the variation in age of onset among individuals, a study shows. The study, ... Read more

November 1, 2018November 1, 2018

Juvenile Huntington’s More Aggressive, Leads to Early Symptoms, Study Reports

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The juvenile form of Huntington’s disease, which affects patients younger than 20, is particularly aggressive and associated with an early onset of symptoms, a retrospective study has found. Based on ... Read more

October 29, 2018October 29, 2018

#NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach

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With the U.S. midterm elections now less than two weeks away, patient advocacy groups are solidly focused on a range of hot-button issues, from the Orphan Drug Tax Credit ... Read more

October 25, 2018October 25, 2018

DNA-based Therapy Reduces Anxious Behavior in Huntington’s Mouse Model, Study Shows

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Suppressing the expression of the defective huntingtin gene using antisense oligonucleotides lowered anxiety-like behavior in a mouse model of Huntington’s disease, a study reports. These compounds were also efficiently delivered into the ... Read more

October 23, 2018October 23, 2018

Gene Therapy VY-HTT01 Can Protect Brain Cells from Damage Caused by HTT Faulty Gene, Results Show

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One-time delivery of Voyager Therapeutics’ lead candidate gene therapy, VY-HTT01, effectively reduced the levels of the faulty gene responsible for Huntington’s disease in important brain areas of non-human large primates. These ... Read more

October 18, 2018October 18, 2018

Advanced Huntington’s Patients Have Marked Difficulties in Driving, Study Shows

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Patients at advanced stages of Huntington’s disease have marked difficulties in controlling vehicles in a driving simulator compared to patients who are at a pre-symptomatic stage or healthy subjects, ... Read more

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