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AAN 2023: Phase 1/2 trial to test AskBio’s gene therapy in patients

Asklepios Biopharmaceutical (AskBio) has launched a first-in-human clinical trial testing AB-1001 — an experimental gene therapy designed to modulate cholesterol metabolism in the brain — in people with Huntington’s disease. The trial is currently recruiting participants at a site in Paris. It is open to adults, ages 18…

A trip to the pharmacy becomes a valuable lesson

In 2018, my wife, Jill, was diagnosed as gene-positive for Huntington’s disease (HD). In the months leading up to her diagnosis, she’d begun experiencing depression and anxiety, as well as other HD symptoms, which started her down the long road of finding helpful medications. At…