The gleaming new Dutch headquarters of the European Medicines Agency (EMA), fronting Domenico Scarlattilaan in Amsterdam’s suburban Zuidas business…
Articles by Larry Luxner
As many as 80 experts from a dozen countries will gather next month in Vienna for the European Conference…
With so much recent publicity surrounding gene therapy, it’s no surprise that the topic was a major focus of the…
Despite skyrocketing healthcare costs, President Trump is committed to protecting the 30 million or so Americans with rare diseases and…
Next month’s annual conference of the National Organization for Rare Disorders (NORD) in Washington, D.C., couldn’t come at a…
Developing gene therapies for rare diseases is one thing. Creating gene-edited “designer babies” is quite another. German legal expert Timo…
Imagine living your whole life with a painful disease so rare that only 25 others worldwide have what you have.
Oklahoma suffers more tornadoes than any other state, has the highest per-capita rate of women in U.S. prisons, ranks second…
A new international consortium based in Paris, and funded largely by the 28-member European Union, intends to speed the diagnosis…
Egypt, the most populous country in the Arab world, has the highest prevalence of Huntington’s disease, yet this nation…