Vaccinex is hosting a business opinion leaders luncheon on Huntington’s disease in New York City today. As part of the program, the company will discuss its Huntington’s therapy VX15/2503 (VX15). The antibody counters semaphoring 4D (SEMA4D), a molecule that regulates the activation and migration of inflammatory cells in the brain. Scientists believe…
The European Medicines Agency (EMA) has granted orphan medicinal product designation to AMT-130, uniQure’s gene therapy candidate for the treatment of Huntington’s disease. AMT-130 is an experimental gene therapy that is being evaluated in studies designed to support an investigational new drug (IND) application with the U.S.
People with Huntington’s disease in the U.K. are pushing for more open communication regarding assisted dying between clinicians, patients, and their families, a small research study indicates. A first-of-its-kind study in the United Kingdom, where assisted dying is illegal, looked into the attitudes of people with the debilitating disease, which…
Taube Philanthropies, a charitable organization from the San Francisco Bay Area, in California, recently donated $750,000 to the Buck Institute for Research on Aging to support a research consortium working on Huntington’s disease. Lisa Ellerby, PhD, is leading the consortium in collaboration with the Taube Neurodegenerative Disease Stem…
The Hereditary Disease Foundation (HDF) raised $900,000 to fund research into Huntington’s disease and other brain disorders during its Nov. 6 “Celebration of 50 Years of Discovery” symposium and gala at New York’s Metropolitan Club. The event included a scientific symposium and a dinner and award ceremony, where winners…
The U.S. Patent and Trademark Office (USPTO) recently notified Mitochon Pharmaceuticals of its allowance on the first patent that the company says will help it proceed with the continued clinical development of MP101 as a treatment for Huntington’s disease (HD) and others. MP101 is one of…
Three Huntington’s disease (HD) patient advocacy organizations in Europe and North America recently launched a collaborative effort to give patients and the HD community more of a voice in clinical research. The newly formed Huntington’s Disease Coalition for Patient Engagement (HD-COPE) aims to give Huntington’s patients a platform to express their…
The U.S. Food and Drug Administration (FDA) has awarded orphan drug status to uniQure’s proprietary candidate for Huntington’s disease (HD), a first in the history of Huntington’s treatment. No approved therapies exist to target the underlying cause of Huntington’s, a disease caused by a mutation in the huntingtin gene .
GeneFo will offer a free webinar on how adding humor to Huntington’s patients’ lives can help improve their symptom management, emotional wellbeing, ability to cope with adversity, and social and work interaction. The webinar, which is aimed at caregivers as well patients, will start at 1 p.m. U.S. Eastern…
Three entities — the Clinical Data Interchange Standards Consortium (CDISC), the Critical Path Institute (C-Path) and the CHDI Foundation (CHDI) — have announced that the Huntington’s disease (HD) Therapeutic Area User Guide (TAUG-HD v1.0) is up for public review through Nov. 10. TAUG-HD v1.0 was developed through the Coalition…
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