• Overcoming Denial in the Face of Huntington’s Disease
  • Austedo to Manage Chorea Safe at Higher Doses, Study Finds
  • To Join or Not to Join, That Is the Question
  • Coalition Will Address Racial Disparities in Rare Disease Communities
  • The Real World Is Precious
  • ‘Hero’ Proteins Protect Other Proteins from Stress, Research Finds
  • Pepinemab Clinical Trial Ongoing; Top-line Results Coming Later this Year
  • A Caregiver’s Biggest Lesson
  • COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say
  • Feeling Helpless Vs. Being Helpful
  • China Approves Austedo for Huntington’s-related Chorea
  • Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe